- 1422959-91-8
- Golodirsen
Golodilsen (SRP-4053) is a phosphodiester morpholine oligomer (PMO) that specifically targets exon 53 of the precursor mRNA of muscular dystrophy protein and can be used in the study of Duchenne muscular dystrophy (DMD).
Golodilsen (SRP-4053) is a phosphodiester morpholine oligomer (PMO) that specifically targets exon 53 of the precursor mRNA of muscular dystrophy protein and can be used in the study of Duchenne muscular dystrophy (DMD).
